Gene therapy is performed by ____.​   a. ​replacing a defective enzyme in an individual with a normal enzyme with the goal of treating a genetic disorder   b. ​transferring a normal or a modified gene into an individual with the goal of treating a genetic defect​   c. ​transferring a mutated gene into an individual with the goal of treating a genetic defect   d. ​replacing a defective gene in an individual with a normal gene with the goal of treating a genetic disorder   e. replacing the genomes of an individual with a brand new set of genomes with the goal of treating a genetic defect​

Q: What would the correct answer for this order question?

A: Gene therapy is a treatment used to correct some genetic diseases by the insertion of new DNA which…

Q: linkage disequilibrium

A: a) Linkage:  Linkage is the phenomenon of certain genes staying together during inheritance…

Q: Please talk about the Different stages at which modification of DNA, mRNA, and protein is possible.

A: The DNA to protein pathway is the mechanism that permits the cell to produce one of the most…

Q: How can we be sure that the insertion of the therapeutic gene does not harm some other necessary…

A: The Food and Drug Administration still has not approved any human gene therapy product. Current gene…

Q: Define the following terms:a. hypochromic effectb. DNA denaturationc. restriction endonucleasesd.…

A: Recombinant DNA is made by combining two or more DNA from other sources. The process depends on the…

Q: organisms

A:

Q: With this gene provided: MuPKS c.1949 C>T (p.R644W) Please provide the following; 1. Name of the…

A: The DNA is formed of two nucleotide chains joined through a hydrogen bond formed between the…

Q: 1) Write one example about mutation in human. 2) Identify if this mutation is harmful or beneficial.

A: A mutation is a term referred to as a change in the DNA sequence. It is a change which occurs in the…

Q: which of these describes the symptoms of the disease(s) caused by mutations in this gene…

A: Mutation in the following gene i.e. XPA gene, causes malfunctioning of DNA repair mechanisms of our…

Q: The first attempts at gene therapy began in 1990 with the treatment of a young girl with a genetic…

A: SCID stands for Severe combined Immunodeficiency. SCID is a group of very rare, life-threatening…

Q: How can you treatment for the genetic disorders by using gene therapy?  Please answer at your own…

A: Gene therapy is a technique for correcting imperfect genes responsible for disease development. Gene…

Q: Cystic Fibrosis is caused by a mutation in the CFTR gene, and an ideal form of treatment would be to…

A: Cystic fibrosis is an inherited life threatening disorder that causes severe damages to lungs,…

Q: Explain an example of a successful gene therapy trial. In your answer be sure to consider: a…

A: SCID is a genetic disorder caused by numerous genetic mutations which are characterized by the…

Q: Below is the genotyping results using PCR and gel electrophoresis for a DNA-binding regulatory…

A: The transcription factor is responsible for binding to the promoter. It leads to proper binding of…

Q: The enzymes mentioned below are used as tools during cloning, DNA sequencing and/or gene therapy.…

A: Enzymes  Enzymes are the protein that use as catalysts in metabolic and catabolic reaction to fasten…

Q: Explain Synthetic Lethal Mutations.

A: The mutation is caused due to alteration occurred in the gene sequence due to either environmental…

Q: The DNA site of a person diagnosed with Sickle Cell Anemia will be:

A: Sickle cell anemia is a genetic disease which occurs due to substitution of glutamic acid by…

Q: Draw a schematic diagram of how we can Treatment Cancer by using gene therapy? Please answer at your…

A: Gene therapy is a technique in which Replacement of a disease-causing gene with a healthy copy of…

Q: Describe some methods used to deliver normal genes to cells for gene therapy treatments.

A: When the treatment of a disease is carried out by transferring genetic material into the cells, it…

Q: When using gene therapy to treat an hereditary disease, the idea is to: A. Introduce the correct…

A: Genes are the functional segment of DNA which encode for proteins.

Q: Discuss the use of gene therapy in treating cancer.

A: Gene therapy involves changing the genetic instructions within a person's cells to treat or prevent…

Q: provide an argument/ what is the relevance of gene therapy in medicine using alziemer disease as an…

A: Gene therapy is a technique in which the gene is modified or edited that is some nucleotides can be…

Q: An unapproved form of gene therapy, known as enhancement gene therapy, can create considerable…

A: Answer: Introduction: Present gene therapy research has fixated on treating persons by directing the…

Q: A. Which genes could be used to monitor the process of the disease? B.  If you worked for a drug…

A: By collecting mRNA samples from patients over the course of four phases, we may analyze the…

Q: The first mutation is thought to occur in utero in most cases of ALL diagnosed before age 5 years…

A: Acute Lymphoblastic Leukemia (ALL) is a type of blood cancer that affects white blood cells. It is…

Q: pick a specific disease that is currently a candidate for gene therapy—(a)briefly describing the…

A: Gene therapy aims at treating the disease at the molecular level, by modifying the genetic material…

Q: In general, all mutations can be considered harmful, because most genetic systems are already…

A: Mutation can be defined as a heritable genetic change in the genetic material of an organism that…

Q: Of those in the following list, which organ(s)/tissue(s) is/are affected by mutations in this gene…

A: Mutations in the following gene gives rise to a genetic disorder known as Xeroderma pigmentosum.…

Q: A. In practice, U.S. [ Select ] ["eugenics", "gene therapy", "recombinant DNA", "population…

A: The human body is a well built machine in which all the organs coordinate together to make it work.…

Q: robes for cloned genes use ____.   a. certain bacteria that glow when they take up the genes   b.…

A: Gene cloning: It is a procedure that makes researchers prepare several similar copies of gene-sized…

Q: Who should be treated by gene therapy? What criteria are used to determine if a person is a…

A: The process of gene therapy is otherwise known as human gene transfer. It accounts for the…

Q: Briefly answer the question: Exome sequencing to identify a mutation that could cause a particular…

A: Primary findings are the testing results which are obtained and provide required information about…

Q: Label this flow chart of mutagenesis: 3 2 |Replication Eppoes mutation! Column A Column B 1. a. DNA…

A: Genetic material is nothing but the sequence of nucleic acids which is called as DNA. It contains…

Q: Define the following terms:a. point mutationb. transition mutationc. transversion mutationd. silent…

A: Any alteration in the DNA sequence is called a mutation. It can occur due to replication errors…

Q: A disease "D" is caused by a combination of genetic and environmental factors. Polymorphisms in…

A: In the progression of the disease and pathogenesis of disease-causing agents genetic and…

Mitochondrial Mutations

A mitochondrion is a cellular organelle that serves as the site for cellular respiration and energy production (ATP or Adenosine Triphosphate). It is a double-membrane-bound organelle and is only present in eukaryotic cells.