Name any one disease for which gene therapy has been proved effective?

Q: How can RNA sequencing (RNA-Seq) and microarrays in Transcriptome analysis find disease genes?

A: Researchers can describe the transcriptional activity (coding and non-coding), concentrate on a…

Q: Describe the methods that are being used to introducegenes into humans for gene therapy.

A: Gene therapy is a clinical field which centers around the usage of the remedial conveyance of…

Q: What is a molecular marker? Give two examples. Discuss why it isgenerally easier to locate and map…

A: Introduction: Molecular markers are specific DNA segments identifiable among others in the whole…

Q: What is ex vivo gene therapy?

A: Gene therapy is the bioengineering technique in which any genetic defect is corrected by altering…

Q: What is the purpose of the activity “Transgenic Manipulation?”

A: Transgenic manipulation During the last couple of decades , considerable progress have been made…

Q: How does an RT-PCR work?

A: RT- PCR is a technique used in genetic studies used for the detection and quantification of mRNA.…

Q: What is one stumbling block in AAV gene therapy in some patients?

A: Biotechnology is technology that utilizes biological systems, living organisms or parts of this to…

Q: What vectors can be used for cloning?

A: Introduction: Vectors are the molecular vehicles used for the transfer of genes of interest into the…

Q: Why is it that the line of treatment for a genetic disease is different from infectious diseases?

A: A disease is a disorder that causes changes in physiological functions and result in specific sign…

Q: Name any two diseases for which transgenic mice are used as model organisms.

A: The transgenic mouse is obtained by the introduction of foreign DNA into the genome of the mouse. It…

Q: How is DNA testing advantageous to paternity cases?   Question 27 options:   a)…

A: DNA paternity testing relies on analyzing specific regions of the DNA molecule called genetic…

Q: Explain why cures of single gene diseases are deficient.

A: Single gene diseases, also known as monogenic disorders, are genetic diseases that are caused by…

Q: There are four possible observations that suggest an error occurred in a PCR reaction: a) Sequence…

A: PCR reaction is a method used to amplify a small sample into millions of small ones which help the…

Q: Explain the use of a marker gene ?

A: Gene is a functional unit of heredity. Marker genes are those genes which are added along with a…

Q: Explain gene-knockout technique.

A: According to the question, we have to provide an explanation of the gene knockout technique.  So,…

Q: What are transgenic Bacteria? Illustrate using any one example?

A: Genetic engineering is the modification of an organism’s genome for a beneficial outcome. Bacteria,…

Q: Which is used for cloning eukaryotic genes but not prokaryotic genes?a) Restriction enzymesb) DNA…

A: Restriction enzymes are the enzymes that cleave the deoxyribonucleic acid (DNA) at specific sites…

Q: What is double-knockout animals (DKOs) ?

A: Gene is the basic unit of heredity of an organism. In most animals, Deoxyribonucleic acid (DNA) is…

Q: What different techniques can be used for transcriptomeanalysis ?

A: The transcriptome is the set of all RNA transcripts including coding and non-coding in an individual…

Q: The inheritance of one or more mutated genes can result in a genetic disease. Some genetic diseases…

A: Inheritance refers to the passing on of traits, characteristics or genetic information from parents…

Q: Which of the following is not associated with gene therapy SCID patients A) utilizes an enzyme to…

A: Severe combined immunodeficiency (SCID): it is an inherited primary immunodeficiency disease (PIDD)…

Q: Explain how PCR/OLA (polymerase chain reaction/oligonucleotide ligation assay) can be used in the…

A: Introduction Sickle cell disorder is a rare condition in which the red blood cells of the individual…

Q: An elderly woman took a prescription medicine to help her to sleep; however, she felt restless all…

A: Sleeping tablets are prescribed to treat insomnia. They fall under the category of…

Q: The majority of direct-to-consumer genetic tests: A) must be obtained through a doctor B) makes…

A: Genetic tests are a type of medical test that looks for changes in genes, chromosomes, or proteins.…

Q: What is artificial transformation used for?

A: Transformation is a process in which an organism acquires exogenous DNA. This process occurs in two…

Q: What is transgenic mutation?

A: Mutation is the sudden heritable changes that occur in the DNA sequences due to error while copying…

Q: What is preimplantation genetic diagnosis?

A: Prenatal diagnosis is performed for the identification of genetic diseases and their predisposition…

Q: Which is the most appropriate example of a product formed by an indirect form of gene therapy? a…

A: The term Gene therapy means treatment that is induced at the gene level. In this therapy,…

Q: Transgenic organisms are generallya) Extinct organismsb) Naturally occurring and endemicc) Produced…

A: Transgenic organisms are also called as genetically modified organism as they have a foreign DNA…

Q: What types of viruses are used for gene therapy, and how are they manipulated to make them useful?

A: Gene therapy is the technique used to cure or prevent the disease by introducing the normal gene in…

Q: How might we, as epidemiologists, increase the validity of genetic studies? What recommendations do…

A: Epidemiology is considered a branch of medical science that deals with the identification and…

Q: For what the first clinical gene therapy was given?

A: Gene therapy is a medical technique in which genes are used for treating and preventing a disease.…

Q: Who created the gene gun?

A: Any of the various substances that are generated by living organisms and cells are called…

Q: The NIH Recombinant DNA Advisory Committee has what responsibility? a) Approving all forms of human…

A: The Recombinant DNA Advisory Committee (RAC) was created by the National Institute of Health (NIH)…

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